Table 4.
GAG concentration in brains of mice treated with gene therapy
| # | Groups | Total GAG | Mean ± SD | DS-HS (%)a |
|---|---|---|---|---|
| 11 |
WT 20w |
1140.4 |
1566 ± 419 |
6.2 |
| 12 |
WT 20w |
1281.2 |
|
9.9 |
| 13 |
WT 20w |
1997.3 |
|
32.1 |
| 14 |
WT 20w |
1849.6 |
|
29.0 |
| 1 |
WT 29w |
NE |
1907 ± 212 |
23.8 |
| 2 |
WT 29w |
2057.0 |
|
NE |
| 3 |
WT 29w |
1757.3 |
|
9.8 |
| 15 |
KO 20w |
2741.0 |
2443 ± 470 |
40.0 |
| 16 |
KO 20w |
2889.3 |
|
48.8 |
| 24 |
KO 20w |
1850.0 |
|
50.0 |
| 25 |
KO 20w |
2290.0 |
|
48.2 |
| 4 |
KO 29w |
4345.0 |
3234 ± 1287 |
49.8 |
| 5 |
KO 29w |
3235.5 |
|
47.7 |
| 26 |
KO 29w |
1429.0 |
|
43.5 |
| 27 |
KO 29w |
3930.0 |
|
57.3 |
| 19 |
KO/IDUA 20w |
1220.2 |
2065 ± 487 |
37.3 |
| 20 |
KO/IDUA 20w |
2323.0 |
|
42.1 |
| 21 |
KO/IDUA 20w |
2404.4 |
|
46.1 |
| 22 |
KO/IDUA 20w |
2296.0 |
|
49.2 |
| 23 |
KO/IDUA 20w |
2083.0 |
|
49.4 |
| 8 |
KO/IDUA 29w |
1656.0 |
1509 ± 364 |
42.6 |
| 9 |
KO/IDUA 29w |
1778.9 |
|
39.8 |
| 10 | KO/IDUA 29w | 1094.2 | 55.6 |
Total GAG is expressed in μg/g dry tissue; (#) Animal identification number;
a % = [DS-HS]/[Total GAG] * 100; NE = non-evaluated; w = week-old.