Table 2.
All ages (N = 87) | Age group 4-7 (N = 10) | Age group 8-12 (N = 30) | Age group 13-18+ (N = 47) | |||||||||||||
---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
|
N |
% |
N |
% |
N |
% |
N |
% |
||||||||
Gender |
|
|
|
|
|
|
|
|
||||||||
Female |
43 |
49% |
4 |
40% |
16 |
53% |
23 |
49% |
||||||||
Male |
44 |
51% |
6 |
60% |
14 |
47% |
24 |
51% |
||||||||
Treated with Agalsidase Alfa |
||||||||||||||||
No |
37 |
43% |
7 |
70% |
17 |
57% |
13 |
28% |
||||||||
Yes |
50 |
57% |
3 |
30% |
13 |
43% |
34 |
72% |
||||||||
FOS MSSI |
||||||||||||||||
Mild (<20) |
81 |
93% |
10 |
100% |
27 |
90% |
44 |
94% |
||||||||
Moderate (20-40) |
3 |
3% |
0 |
0% |
1 |
3% |
2 |
4% |
||||||||
Missing | 3 | 3% | 0 | 0% | 2 | 7% | 1 | 2% |