Table 1.
Patient no. | MPS type | Gender | Age at diagnosisa | Age at the therapy onseta |
---|---|---|---|---|
1 | MPS IIIA | Female | 0 y 10 m | 7 y 0 m |
2 | MPS IIIA | Male | 7 y 10 m | 11 y 1 m |
3 | MPS IIIB | Female | 5 y 0 m | 6 y 6 m |
4 | MPS IIIA | Female | 3 y 6 m | 3 y 6 m |
5 | MPS IIIA | Male | 1 y 8 m | 2 y 0 m |
6 | MPS IIIA | Male | 3 y 0 m | 4 y 7 m |
aAge is provided in years (y) and months (m)