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. Author manuscript; available in PMC: 2013 Sep 13.
Published in final edited form as: Expert Opin Pharmacother. 2013 Mar;14(4):435–447. doi: 10.1517/14656566.2013.775250

Table 2.

Major clinical trials in pharmacotherapy of kidney stones

Authors Year (ref.) Treatment Population Studied Study Duration
(Years)
Treated/Placebo Design Recurrence (%)
Treated/Control
Finding
RR
Thiazide Therapy
Brocks
1981 (38)
Bendroflumethiazide
2.5 mg TID
CaSF (n=62) 1.6 33/29 RCD 24/16 NS
Scholz
1982 (39)
HCTZ 25 mg BID CaSF (n=51) 1 25/26 RCD 24/23 NS
Laerum
1984 (30)
HCTZ 25 mg BID CaSF (n=50)
(M/F=38/12)
3 25/25 RCD 20/48 0.39
Wilson
1984 (31)
HCTZ 100 mg daily CaSF (n=44) 2.8 23/21 RC 21/44 0.48
Robertson
1985 (32)
Bendroflumethiazide
2.5 mg TID
CaSF (n=22) 3 to 5 13/9 RC 0.38
Mortensen
1986 (37)
Bendroflumethiazide
2.5 mg TID + KCl TID
CaSF (n=22)
(M=22)
2 12/10 RCD 40/40 NS
Ettinger
1988 (33)
Chlorthalidone
25/50 mg daily
CaOx SF (n=73)
(M/F=63/10
3 19(25mg)/
23(50mg)/
31(placebo)
RCD 14/46 0.23
Ohkawa
1992 (34)
Triclormethiazide
4mg daily
CaSF (n=175) 2.1 to 2.2 82/93 RC 0.42
Borghi
1993 (35)
Indapamide
2.5mg daily
CaOx SF (n=75) 3 43/14 RCD 15/43 0.21
Fernandez-Rodriguez
2006 (36)
HCTZ 50 mg daily CaSF (n=100) 3 50/50 RC 0.56
Citrate Therapy
Barcelo
1993 (50)
Potassium Citrate
30-60 mEq/d
Hypocit CaSF (n=57)
(M/F=25/32
3 18/20 RCD 28/80
Ettinger
1997 (51)
Potassium Mg Citrate
60 mEq/d
CaOx SF (n=64)
(M/F=50/14)
3 31/33 RCD 13/64
Hofbauer
1994 (52)
Sodium K Citrate
Variable dose to
Keep urine pH 7-7.2
CaOX SF (n=50)
M/F=31/19
3 25/25 RCD 69/73 NS

CaOx, calcium oxalate; SF, stone former; M, male; F, female; RC, randomized controlled; RCD, randomized controlled double blind; HCTZ, hydrochlorothiazide; Hypocit, hypocitraturic; RR, relative risk; NS, no significance