Table 1.

Subject demographics upon study enrollment.

		N	Minimum	Maximum	Mean (SD)
Age (years)	All patients	85	44.8	83.9	65.7 (±8.5)
	Male	64	44.8	83.9	66.3 (±8.1)
	Female	21	49.4	80.8	63.9 (±9.6)
Height (cm)	All patients	81	152.4	195.6	176.2 (±8.8)
	Male	61	165.1	195.6	179.8 (±6.1)
	Female	20	152.4	177.8	165.2 (±6.7)
Weight (lbs.)	All patients	81	98	270	184.0 (±36.9)
	Male	61	135	270	196.3 (±29.8)
	Female	20	98	225	146.5 (±31.1)
Onset of symptoms to diagnosis (years)	All patients	77	<1	16	3.2 (±3.1)
	Male	57	<1	16	3.0 (±3.1)
	Female	20	<1	12	4.0 (± 32)
Diagnosis to visit (years)	All patients	78	<1	16	5.1 (±3.5)
	Male	58	<1	16	5.0 (±3.5)
	Female	20	1	12	5.3 (±3.6)
Onset of symptoms to visit (years)	All patients	77	2	20	8.2 (±4.5)
	Male	57	2	20	7.9 (±4.3)
	Female	20	3	20	9.1 (±5.0)