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. Author manuscript; available in PMC: 2014 Jan 6.
Published in final edited form as: OA Autism. 2013 Jun 19;1(2):14. doi: 10.13172/2052-7810-1-2-610

Table 1.

Chromatin genes implicated in autism spectrum disorders

Gene
name
aliases Human
chrom
location
Human
disease
Protein
function
Interacting
proteins
refs
MECP2 Methyl CpG binding protein 2, ARBP Xq28 Rett syndrome (RTT), autism (rare mutation or aberrant methylation) Binds mCpG, repression, chromatin dynamics Sin3a, HDAC, ATRX, YB1, SMC1A 9, 4246
ATRX RAD54, XH2 Xq21.1 thalassemia, intellectual disabilities SWI/SNF chromatin remodeling, ATPase/helicase domain MeCP2, SMC1A 13, 47
H2AFY MACROH2A1.1 5q31.1 Autism (association) Histone H2 variant, X-chromosome inactivation HDAC1, PARP1 8, 48
SMC1A Cohesin, CDLS2 Xp11.22 Cornelia de Lange syndrome (CDLS) Chromosome cohesion ATRX, SMC3, MeCP2, CTCF 13
MACROD2 20p12.1 Autism (association) O-acetyl-ADP-ribose deacetylase, binds this metabolite from histone deacetylation 11
KDM5C JARID1C, SMCX Xp11.22 ASD, ID (rare mutations) Histone demethylase of H3K4, gene repression HDAC, REST 4952
MBD1 CXXC3 18q21 Autism (rare mutations), also rare variants in related genes MBD4, MBD5 Binds mCpG, links mCpG to H3K9me3 SETDB1, AFT7IP 9, 53, 54
ARID1B BAF250B 6p25.3 Coffin-Siris syndrome (CSS), mental retardation autosomal dominant type 12 (MRD12), autism (rare) Component of SWI/SNF chromatin remodeling complex, AT-rich binding domain SWI/SNF complex proteins in neuronal BAF complex (nBAF) 14, 15
SMARCC1 BAF155 3p31.21 Autism (rare mutation) Component of SWI/SNF chromatin remodeling complex, and nBAF ARID1A, ARID1B, SMARCC2, 5
SMARCC2 BAF170 12q13.2 Autism (rare mutation) Component of SWI/SNF chromatin remodeling complex, and nBAF ARID1A, SMARCC1, HDAC1/2 5
JMJD1C TRIP8 10q21.3 Autism (rare mutation, translocation, abnormal methylation) Histone demethylase for H3K9, hormone-dependent transcriptional activation Thyroid hormone receptor, androgen receptor 5, 25, 55, 56
CHD8 AUTS18 14q11.2 autism (rare mutation), also rare autism variants in family members CHD1, CHD3, CHD7) ATP-dependent chromatin helicase, negative regulator of Wnt signaling pathway by regulating beta-catenin (CTNNB1) p53, histone H1, CTNNB1, CTCF, MLL complex proteins WDR5, RBBP5, CHD7 (mutated in CHARGE) 5, 6, 16