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. 2014 Apr 25;1:184–196. doi: 10.1016/j.ymgmr.2014.04.001

Table 3.

BMI of patients with MPS II undergoing therapy.


HSCT
(kg/m2)
t-Test to untreated group
ERT
(kg/m2)
t-Test to untreated group
t-Test between two treatment groups
Age (years) n Mean SD p n Mean SD p p
9.5 months 1 16.15
1 y 1 16.29
1.5 y 4 17.49 0.41 0.15
2 y 1 20.37 4 18.83 1.07 0.80
3 y 1 18.60 5 18.33 0.36 0.05
4 y 4 20.27 3.87 0.46 6 19.40 0.95 0.19 0.69
5 y 8 19.84 2.87 0.53 5 19.27 1.73 0.85 0.66
6 y 12 21.40 4.98 0.28 8 18.83 2.09 0.43 0.13
8 y 9 21.32 5.56 0.70 11 18.83 1.42 0.06 0.22
10 y 8 21.56 6.26 0.51 7 18.99 2.70 < 0.01 0.32
12 y 9 21.68 4.96 0.56 7 22.02 3.23 0.62 0.87
14 y 6 20.81 3.98 0.39 1 22.74
16 y 4 19.20 1.66 0.04
18 y 2 17.57