Table 3.
BMI of patients with MPS II undergoing therapy.
HSCT (kg/m2) |
t-Test to untreated group |
ERT (kg/m2) |
t-Test to untreated group |
t-Test between two treatment groups |
|||||
---|---|---|---|---|---|---|---|---|---|
Age (years) | n | Mean | SD | p | n | Mean | SD | p | p |
9.5 months | 1 | 16.15 | |||||||
1 y | 1 | 16.29 | |||||||
1.5 y | 4 | 17.49 | 0.41 | 0.15 | |||||
2 y | 1 | 20.37 | 4 | 18.83 | 1.07 | 0.80 | |||
3 y | 1 | 18.60 | 5 | 18.33 | 0.36 | 0.05 | |||
4 y | 4 | 20.27 | 3.87 | 0.46 | 6 | 19.40 | 0.95 | 0.19 | 0.69 |
5 y | 8 | 19.84 | 2.87 | 0.53 | 5 | 19.27 | 1.73 | 0.85 | 0.66 |
6 y | 12 | 21.40 | 4.98 | 0.28 | 8 | 18.83 | 2.09 | 0.43 | 0.13 |
8 y | 9 | 21.32 | 5.56 | 0.70 | 11 | 18.83 | 1.42 | 0.06 | 0.22 |
10 y | 8 | 21.56 | 6.26 | 0.51 | 7 | 18.99 | 2.70 | < 0.01 | 0.32 |
12 y | 9 | 21.68 | 4.96 | 0.56 | 7 | 22.02 | 3.23 | 0.62 | 0.87 |
14 y | 6 | 20.81 | 3.98 | 0.39 | 1 | 22.74 | – | – | |
16 y | 4 | 19.20 | 1.66 | 0.04 | |||||
18 y | 2 | 17.57 | – | – |