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Indications addressed by gene therapy clinical trials up to January 2014.
| Ranking | Indication | Number of trials (n) | Percentage with respect to total gene therapy clinical trials (%) |
|---|---|---|---|
| 1 | Cancer diseases | 1274 | 63.8 |
| 2 | Monogenic diseases | 178 | 8.9 |
| 3 | Infectious diseases | 164 | 8.2 |
| 4 | Cardiovascular diseases | 162 | 8.1 |
| 5 | Healthy volunteers | 52 | 2.6 |
| 6 | Gene marking | 50 | 2.5 |
| 7 | Neurological diseases | 37 | 1.9 |
| 8 | Other diseases | 35 | 1.8 |
| 9 | Ocular diseases | 31 | 1.6 |
| 10 | Inflammatory diseases | 13 | 0.7 |
