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. Author manuscript; available in PMC: 2014 Aug 27.
Published in final edited form as: Am J Med Genet C Semin Med Genet. 2011 Apr 14;0(2):136–146. doi: 10.1002/ajmg.c.30294

TABLE II. Current Status of Ras/MAPK Small Molecules for Clinical Trials.

Agent Target Company/partner Status
RAS modulation
 Lonafarnib (Sarasar) Farnesyl transferase Merck/Schering-Plough Phase II
 Tipifarnib (Zarnestra) Farnesyl transferase Johnson & Johnson Phase I/II
 Salirasib RAS antagonist Concordia Phase I/II
RAF inhibition
 Sorafenib (Nexavar) RAF/multi-targeted Onyx/Bayer Pharmaceuticals Approved
 RAF265 RAF/multi-targeted Novartis Phase I/II
 PLX4032 BRAF Plexxikon/Roche Phase III
 PLX5568 BRAF Plexxikon/Roche Phase I/II
 GSK2118436 BRAF GlaxoSmithKline Phase I/II
 XL281 (BMS908662) BRAF Exelixis/Bristol-Myers Squibb Phase I/II
MEK inhibition
 CI-1040 MEK Pfizer Terminated
 PD0325901 MEK Pfizer On Hold
 AZD6244 (ARRY-886) MEK Array/AstraZeneca Phase I/II
 AZD8330 (ARRY-704) MEK Array/AstraZeneca Phase I/II
 ARRY-162 MEK Array/Novartis Phase I/II
 ARRY-300 MEK Array/Novartis Phase I/II
 RDEA119 MEK Ardea/Bayer Phase I/II
 RDEA436 MEK Ardea/Bayer Phase I/II
 E6201 MEK Eisai Phase I/II
 GSK1120212 MEK GlaxoSmithKline Phase I/II
 WX554 MEK Wilex AG Phase I/II
 GDC-0973 MEK Genentech Phase I/II
 AS703026 MEK EMD Serono Phase I/II
 RG7168 (CH4987655) MEK Chugai/Roche Phase I/II
 TAK-733 MEK Takeda/Millenium Phase I/II