Table 2.
Number of patients with somatic signs or symptoms assessed as “improved” on enzyme replacement therapy
| Number of signs/symptoms improved on ERT | Number of patients (n = 22) |
|---|---|
| 7 | 1 |
| 6 | 4 |
| 5 | 13 |
| 4 | 4 |
| Fewer than 4 | 0 |
ERT enzyme replacement therapy
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