Table 2.
Individually significant genes identified from the analysis of de novo mutations in ASD cases. Genes with multiple loss-of-function (LoF) de novo mutations across 1,078 ASD cases. LoF mutations include nonsense, frameshift, and splice site-disrupting mutations. “# LoF Expected” refers to the expected number of de novo LoF mutations based on the probability of mutation for the gene as determined by our model. The genome-wide significance threshold is 1×10−6
Gene | Mutations | # LoF Observed | # LoF Expected | p-value |
---|---|---|---|---|
DYRK1A | nonsense, splice, frameshift | 3 | 0.0072 | 6.15E-08 |
SCN2A | nonsense, nonsense, frameshift | 3 | 0.0178 | 9.20E-07 |
CHD8 | nonsense, splice, frameshift | 3 | 0.0221 | 1.76E-06 |
KATNAL2 | splice, splice | 2 | 0.0049 | 1.19E-05 |
POGZ | frameshift, frameshift | 2 | 0.0133 | 8.93E-05 |
ARID1B | frameshift, frameshift | 2 | 0.0178 | 1.57E-04 |