Table 2.
Abbreviation | Study Group | Sample size (person measurements) | SMA Type |
---|---|---|---|
CHOP-INTEND | PNCRN* | 132 | 1, 2 |
EK2 | Danish Muscle Group, Italian SMA Group, UK Smartnet, PNCRN | 154 | 1, 2, 3 |
GMFM | AmSMART PNCRN | 554 | 1, 2, 3 |
HFMS | Italian SMA Group, Hammersmith Clinic/SMAF | 390 | 2, non-ambulant 3 |
HFMSE | PNCRN | 579 | 1, 2, 3 |
MFM | MFM Study Group | 143 | 1, 2, 3 |
MHFMS | Project Cure, SMAF- BforSMA Study | 401 | 2, 3 |
NSAA for SMA | Smartnet – Part of North Star Clinical Network, UK | 48 | 3 |
TIMPSI | Project Cure | 83 | 1 |
PNCRN, Pediatric Neuromuscular Clinical Research Network for SMA.