Table 1. Clinical data of all SMA patients sorted by age.
ID | Type | Age at inclusion (years) | Weight (kg) | Height (cm) | Time spent in the wheelchair (months) | Arthrodesis | FVC (%) | NNV | Tracheo- stomy | Brooke score (#) |
---|---|---|---|---|---|---|---|---|---|---|
703 | SMA III | 8.3 | 27 | 121 | 45 | no | 79 | no | no | 2 |
203 | SMA II | 10.7 | 23 | 134 | 129 | no | 43 | no | no | 3 |
502 | SMA III | 10.7 | 57 | 163 | NA | no | 69 | no | no | 2 |
708 | SMA II | 11.2 | 49 | 140 | 135 | no | NA | no | no | 4 |
323 | SMA II | 12.4 | 25 | NA | 149 | yes | 49 | yes | no | 2 |
326 | SMA II | 12.5 | 50 | 159 | 151 | yes | 39 | yes | no | 5 |
321 | SMA II | 13.2 | 22 | 146 | 158 | yes | 22 | yes | no | 4 |
909 | SMA II | 13.6 | 37 | 145 | 163 | yes | NA | no | no | 2 |
709 | SMA II | 13.8 | 42 | 147 | 165 | yes | 27 | yes | no | 4 |
318 | SMA II | 15.3 | 52 | 161 | 184 | yes | 70 | no | no | 3 |
315 | SMA II | 15.4 | 37 | 141 | 185 | yes | 24 | yes | no | 6 |
320 | SMA II | 15.5 | 37 | 155 | 187 | yes | 16 | no | no | 5 |
512 | SMA II | 16.1 | 50 | 149 | 193 | yes | 24 | yes | no | 6 |
907 | SMA II | 16.6 | 47 | 150 | 199 | yes | NA | yes | no | 4 |
506 | SMA III | 17.5 | 117 | 154 | 90 | NA | 48 | no | no | 3 |
908 | SMA II | 18.9 | 29 | 130 | 227 | yes | 31 | no | no | 4 |
503 | SMA III | 19.9 | 30 | 175 | 143 | yes | NA | no | no | 3 |
107 | SMA III | 21.8 | 65 | 179 | 82 | no | 100 | no | no | 3 |
121 | SMA II | 24.8 | NA | NA | 298 | yes | 16 | no | no | 5 |
905 | SMA II | 26.0 | 40 | 158 | 312 | yes | NA | no | yes | 3 |
118 | SMA III | 27.4 | 51 | 162 | 149 | no | 78 | no | no | 3 |
120 | SMA III | 29.9 | 52 | 163 | 311 | yes | NA | NA | NA | 5 |
113 | SMA II | 31.0 | 35 | 150 | 372 | NA | NA | NA | NA | 3 |
FVC—Forced vital capacity (% of predicted values), NNV—nasal nocturnal ventilation, NA- not available.