Table 1. Characteristics of patients enrolled in NMTRC 002.

Enrollment	N
Total Enrolled	21
Total Received Drug	21
Evaluable	N (%)
Efficacy Evaluable	18 (86)
Safety Evaluable	21 (100)
Age	Years
Mean	8.75
Median	9
Sex	N (%)
Male	14 (67)
Female	7 (33)
Race	N (%)
Caucasian	14 (67)
Hispanic	3 (14)
Black or African American	2 (9.5)
More than one race or unknown	2 (9.5)