Table 2.
Medians and interquartile ranges for lyso-SM-509 in ng/ml for all investigated sub-cohorts
| n | Lyso-SM-509 in ng/ml | |
|---|---|---|
| NPC1 patients | 110 | 6.7 (3.4-10.3) |
| NPC1 carriers | 63 | 0.4 (0.2-0.9) |
| NP- A/B patients | 21 | 29.4 (14.8-40.0) |
| NP- A/B carrier | 5 | 0.09 (0.04-0.16) |
| Healthy controls | 43 | 0.04 (0.03-0.06) |