Figure 2.
Disease-specific change of Pompe disease iPSCs. (a) Mutation analysis shows compound heterozygote mutation (c.796 C>A and c.1316 T>A). (b) Electron microscopy of iPS cell lines (Pompe-1, Pompe2, Pompe3, and control). Arrow is demonstrating accumulated glycogen. Upper scale bar, 5 µm; lower scale bar, 1 µm. (c) GAA enzyme assay of iPS cell lines (Control, Pompe1, Pompe2, and Pompe3). Data were expressed as means ± SEM. (d) Glycogen assay of iPS cell lines (Control, Pompe1, Pompe2, and Pompe3). Data were expressed as means ± SEM.
