Table 3.
Demographic and Clinical Parameters of CN IPD Cohort
| Group | Patient | Gender | Race | Age at ERT† (months) |
Baseline invasive ventilation (Y/N) |
Baseline LVMI (g/m2) |
Age at death/current age (months) |
Deceased (Y/N) |
|---|---|---|---|---|---|---|---|---|
| HSAT | 1 | M | W | 3.5 | N | 253.0 | 50.2 | Y |
| 2 | M | B | 2.8 | N | 160.0 | 44.8 | Y | |
| 3 | M | A | 3.9 | N | 157.2 | 14.7 | Y | |
| 4 | F | A | 2.7 | N | 246.7 | 23.3 | Y | |
| 5 | F | W | 6.1 | N | N/A | 25.5 | Y | |
| 6 | F | B | 1.8 | N | 153.0 | 32.0 | Y | |
| 7 | M | B | 5.6 | N | 202.1 | 45.0 | Y | |
| 8 | F | W | 1.8 | N | 233.4 | 44.6 | Y | |
| 9 | M | W | −0.3 | N | 89.0 | 18.0 | Y | |
| 10 | M | W | 3.4 | N | 200.9 | 92.0 | N | |
| 11 | F | B | 8.9 | N | 175.0 | 33.2 | Y | |
| 12 | M | W | 1.6 | N | 141.0 | 45.8 | Y | |
| 13 | M | A | 4.0 | N | N/A | 19.0 | Y | |
| SIT | 14 | M | B | 7.5 | N | N/A | 84.7 | N |
| 15 | F | A | 3.7 | N | 203.1 | 27.1 | Y | |
| 16 | F | B | 0.3 | N | 141.5 | 45.0 | Y | |
| 17 | F | A | 16.4 | N | N/A | 65.0 | N | |
| LT | 18 | F | B | −0.3 | N | 191.1 | 55.4 | N |
| 19 | F | W | 3.3 | N | N/A | 77.8 | N | |
| 20 | M | W | −0.8 | N | N/A | 89.2 | N |
†
Age at ERT corrected by gestational age
HSAT, high sustained antibody titers; LT, low titers; SIT, sustained intermediate titers; ERT, enzyme replacement therapy; LVMI, left ventricular mass index; M, male; F, female; W, White; B, Black; A, Asian; N/A, not available; Y, yes; N, no