Subject area	Biology
More specific subject area	Inborn errors of metabolism
Type of data	Text files, tables, figures
How data was acquired	Clinical evaluations, magnetic resonance imaging, nerve conduction studies, spirography, lumbar spinal puncture
Data format	Raw, processed
Experimental factors	Subjects were treated with intrathecal laronidase, and pre- and post-treatment data are presented
Experimental features	Clinical data are presented descriptively. Adverse events were tabulated based on subject reporting. Magnetic resonance imaging data were scored for spinal cord compression, hydrocephalus, white matter hyperintensities, and cystic or cribriform changes. Pulmonary function tests, cerebrospinal fluid opening pressure and somatosensory evoked potentials were obtained in standard clinical fashion.
Data source location	N/A (multicenter clinical trial)
Data accessibility	N/A