| Gene therapy |
Human clinical trial |
RPE65 delivered by Adeno-associated Virus (AAV) |
(263) |
| Mouse model |
CHM delivered by Adeno-associated Virus (AAV) |
(264) |
| Human clinical trial |
CHM delivered by Adeno-associated Virus (AAV) |
(270) |
| In vitro model |
CEP290 delivered by Lentivirus vector |
(271) |
| Rat model |
MERTK delivered by Adeno-associated Virus (AAV) |
(272) |
| Mouse model |
CRB1 and CRB2 delivered by Adeno-associated Virus (AAV) |
(273) |
| Cell replacement |
Rat model |
Human RPC transplantation restores mature rat retina cells |
(274) |
| Mouse model |
Adult mouse iPSC differentiate into photoreceptors |
(267) |
| Mouse model |
RPCs differentiate and integrate into functional photoreceptors |
(269) |
| Mouse model |
RPCs differentiate into photoreceptors |
(268) |
| Retinal implants |
Clinical trials |
Argus II Retinal Prosthesis System |
(260,261) |
