Table 1. Multifunctional nanoparticles for preclinical gene delivery studies.
Functionalization | Delivery systems | Advantages |
---|---|---|
PEGylation | PEG-βCD; PEG-PEI | Enhanced of stabilization; prevention of protein absorption; improved circulation time39,40 |
Targeting | RGD-HA-PEI-PBLG; R-PEG20C; transferrin-lipid | Enhanced gene target efficacy in vivo44,48,51 |
Stimulus response | pH sensitive; light sensitive; redox sensitive | Enhanced gene target efficacy in vivo52–54 |
Cell penetrating | p(DAHa-E/APIb) | Cross cell membrane; enhanced cellular uptake58 |
Endosome escaping | (Arg)7-FI-PNA | Cross cell membrane; improved endosomal escaping59 |
Nuclear localization | PC/pDNA/NLS; VKRKKKP-R8 | Nuclear localization62,63 |
βCD, β-cyclodextrin; NLS, nuclear localization sequence; PC, β-cyclodextrin and polyethylenimine; PEI, polyethylenimine; R-PEG20C, cRGD-PEG-PAsp(DET)-cholesteryl.