Table 1. Primary fibroblast lines and age-adjusted neurological severity score.
| Cell line | Age-adjusted neurological severity score |
|---|---|
| WT1 | NA |
| WT2 | NA |
| GM0565 (iPS) | NA |
| GM03123 (iPS) | Not available |
| NPC5 | 1.4 |
| NPC6 (iPS) | 0.5 |
| NPC9 (iPS) | 6 |
| NPC21 | 3.8 |
| NPC24 | 1.6 |
| NPC25 | 6 |
| NPC57 | 7.7 |
| NPC61 | 1.4 |
| NPC66 | 0.4 |
| NPC72 | 0.8 |
| NPC76 | 2.2 |
| NPC77 | 0a |
Abbreviation: NA, not applicable.
Subject evaluated at <1 year of age.