Table 1. Primary fibroblast lines and age-adjusted neurological severity score.
Cell line | Age-adjusted neurological severity score |
---|---|
WT1 | NA |
WT2 | NA |
GM0565 (iPS) | NA |
GM03123 (iPS) | Not available |
NPC5 | 1.4 |
NPC6 (iPS) | 0.5 |
NPC9 (iPS) | 6 |
NPC21 | 3.8 |
NPC24 | 1.6 |
NPC25 | 6 |
NPC57 | 7.7 |
NPC61 | 1.4 |
NPC66 | 0.4 |
NPC72 | 0.8 |
NPC76 | 2.2 |
NPC77 | 0a |
Abbreviation: NA, not applicable.
Subject evaluated at <1 year of age.