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. Author manuscript; available in PMC: 2016 Sep 7.
Published in final edited form as: Nat Biotechnol. 2016 Mar 7;34(4):424–429. doi: 10.1038/nbt.3513
AAVS1 ZFN SBS#30035 (NELD):
1 MDYKDHDGDY KDHDIDYKDD DDKMAPKKKR KVGIHGVPAA MAERPFQCRI CMRNFSRSDH
61 LSRHIRTHTG EKPFACDICG RKFATSGHLS RHTKIHTGSQ KPFQCRICMR NFSYNWHLQR
121 HIRTHTGEKP FACDICGRKF ARSDHLTTHT KIHTGSQKPF QCRICMRNFS HNYARDCHIR
181 THTGEKPFAC DICGRKFAQN STRIGHTKIH LRGSQLVKSE LEEKKSELRH KLKYVPHEYI
241 ELIEIARNST QDRILEMKVM EFFMKVYGYR GKHLGGSRKP DGAIYTVGSP IDYGVIVDTK
301 AYSGGYNLPI GQADEMERYV EENQTRDKHL NPNEWWKVYP SSVTEFKFLF VSGHFKGNYK
361 AQLTRLNHIT NCNGAVLSVE ELLIGGEMIK AGTLTLEEVR RKFNNGEINF RS*
AAVS1 ZFN SBS#30054 (CKKR):
1 MDYKDHDGDY KDHDIDYKDD DDKMAPKKKR KVGIHGVPAA MAERPFQCRI CMRNFSDRSN
61 LSRHIRTHTG EKPFACDICG RKFALKQHLT RHTKIHTHPR APIPKPFQCR ICMRNFSTSG
121 NLTRHIRTHT GEKPFACDIC GRKFARRDWR RDHTKIHTGS QKPFQQCRICM
RNFSQSSHLT
181 RHIRTHTGEK PFACDICGRK FARLDNRTAH TKIHLRGSQL VKSELEEKKS ELRHKLKYVP
241 HEYIELIEIA RNSTQDRILE MKVMEFFMKV YGYRGKHLGG SRKPDGAIYT VGSPIDYGVI
301 VDTKAYSGGY NLPIGQADEM QRYVKENQTR NKHINPNEWW KVYPSSVTEF KFLFVSGHFK
361 GNYKAQLTRL NRKTNCNGAV LSVEELLIGG EMIKAGTLTL EEVRRKFNNG EINF*
HHS Vulnerability Disclosure