Table 1.
Pivotal study (excluding ramp-up) | Extension study | |||
---|---|---|---|---|
Age groupa (years) | Number of subjects treated | Number of infusions administered | Number of subjects treated | Number of infusions administered |
<18 | 22 | 310 | 15 | 364 |
≥18 | 59 | 819 | 48 | 1236 |
Total | 81 | 1129 | 63 | 1600 |
aAge at screening in pivotal study