Table 2.
Therapeutic Target | Transgene | Route | Vector | Number of Patients | Phase | Procedure | Status | Results | End Points | Follow-Up | Reference/Identifier |
---|---|---|---|---|---|---|---|---|---|---|---|
Heart failure | SERCA2a | intracoronary | AAV1 | 9 | 1,2 | primary treatment | completed | positive | safety, walk test, angina class | 1 year | [45] |
Heart failure | SERCA2a | intracoronary | AAV1 | 39 | 2 | primary treatment | completed | positive | walk test, hospitalizations, angina class | 3 years | [46] NCT00454818 |
Heart failure | SERCA2a | intracoronary | AAV1 | 250 | 2b | primary treatment | completed | N/A | time to recurrent event | 1 year | [47] NCT01643330 |
Heart failure | SERCA2a | intracoronary | AAV1 | 24 | 1,2 | LVAD | enrolling | N/A | safety, walk test, angina class | N/A | NCT00534703 |
Heart failure | AC6 | intracoronary | adenovirus | 72 | 1,2 | primary treatment | enrolling | N/A | treadmill test, ECHO | N/A | [48] NCT00787059 |
Heart failure | SDF-1 | intramyocardial | plasmid | 93 | 2 | primary treatment | completed | no effect | walk test, angina class | 4 mo | [49] NCT01643590 |
AAV = adeno-associated virus; AC6 = adenylyl cyclase type 6; ECHO = echocardiography; LVAD = left ventricular assist device; N/A = not available; NCT = clinicaltrals.gov.identifier; SDF-1 = stromal-derived factor 1; SERCA2a = sarcoplasmic reticulum adenosine triphosphatase isoform 2a.