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. 2016 Nov;5(4):308–313. doi: 10.5582/irdr.2016.01025

Table 3. Orphan drug programs run by Chinese drug companies.

Company Drug name Indication Stage of development
Chipscreen Chidamide PTCL launched in China
Shanghai Genomics Aisi Rui, Etuary IPF launched in China
Hua Medicine HME01 PD-LID, FXS preclinical
Prosit Sole Biotechnology multiple products chronic norovirus infection, articular cartilage injury, refractory gout, lupus renal failure & uremia preclinical

FXS, fragile X syndrome; IPF, idiopathic pulmonary fibrosis; PD-LID, Parkinson's disease — L-dopa-induced dyskinesia; PTCL, peripheral T-cell lymphoma.