2′OMe	2′-O-methyl
2′MOE	2′-O-methoxyethyl
AAV	Adeno-associated virus
AO	Antisense oligonucleotide
BMD	Becker muscular dystrophy
CFTR	Cystic fibrosis transmembrane conductance regulator
CyPA	Cyclophilin A
dKO	Double knock out
DM1	Myotonic dystrophy type 1
DMD	Duchenne muscular dystrophy
DMPK	Dystrophia myotonica protein kinase
DNA	Deoxyribonucleic acid
ESE	Exonic splicing enhancer
ESS	Exonic splicing silencer
FDA	Food and drug administration
GAA	Acid α-glucosidase
GFP	Green fluorescent protein
GRMD	Golden retriever muscular dystrophy
HD	Huntington’s disease
HDE	Histone downstream element
hDMD	Human DMD
HIV	Human immunodeficiency virus type 1
hnRNPA1	Heterogeneous nuclear ribonucleoprotein A1
IM	Intramuscular
ISE	Intronic splicing enhancers
ISS	Intronic splicing silencers
IV	Intravenous
LNA	Locked nucleic acid
LV	Lentivirus
MBNL1	Muscleblind-like protein 1
MLV	Murine leukemia viruses
PMO	Phosphorodiamidate morpholino oligomers
PNA	Peptide nucleic acid
PPMO	Peptide phosphorodiamidate morpholino oligomers
rAAV	Recombinant Adeno-associated virus
RCL	replication competent lentiviruses
RCR	replication competent retroviruses
RNA	Ribonucleic acid
RYR1	Type 1 ryanodine receptor
scAAV	Self-complementary adeno-associated virus
SMA	Spinal muscular atrophy
snRNA	Small nuclear RNA
snRNP	Small nuclear ribonucleoproteins
SR protein	Serine/arginine-rich protein
UTR	Untranslated transcribed region
VP	Viral protein