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. Author manuscript; available in PMC: 2018 Jan 1.
Published in final edited form as: Handb Exp Pharmacol. 2017;242:271–307. doi: 10.1007/164_2016_78

Table 2.

Current non-VEGF targets in clinical trials

Drug Drug target Disease target Clinicaltrials.gov ID Phase Number patients
Fractalkine (FKN) CX3C chemokine PDR NCT00728598 1, completed 1998   30
OC-10X tubulin inhibitor PDR, AMD NCT01869933   1   10
Fovista (E10030) Anti-PDGF-B AMD NCT02591914
NCT02214628
NCT01089517
NCT01944839
  1
  2
  2
 3,R
  25
100
449
622
Palomid 529 TORC1/2inhibitor of mTOR AMD NCT01033721
NCT01271270
  1
  1
  13
    5
AdGVPEDF.11D PEDF AMD NCT00109499   1
Sirolimus mTOR IL-2 AMD NCT00766337   2   62
Everolimus (RAD001) mTOR AMD NCT00857259   2  16, terminated
PF-04523655 Block RTP801 mTOR DME
AMD
NCT01445899
NCT00713518
  2
  2
258
152
ARC1905 Inhibit complement C5 aptamer AMD NCT00709527   1   60
iSONEP S1P lipid AMD NCT01414153   2 158
ASP8232 Vascular adhesion protein-1 inhibitor DME NCT02302079   2   96
hI-con1 Factor VIIa inhibitor AMD NCT02358889   2   88
Tocilizumab Antibody IL-6 DME NCT02511067   2   66
iCo-007 inhibitor C-raf DME NCT01565148   2 208
Pf-04634817 CCR2/5 antagonist DME NCT01994291   2 212
ATG003 (mecamylamine) Tubulin depolymerize, tight junction disruption AMD NCT00607750   2   60
RO6867461 DME
AMD
NCT02699450
NCT01941082
  2
  1
150, R
Luminate (ALG-1001) αVβ3 and αVβ5 integrin inhibitor DME NCT02348918   2 150
Apremilast (CC-10004) Inhibit PDE4 (breaks down cAMP) Behcet’s NCT00866359
NCT02307513
  2
  3
111
204
Efalizumab Bind CD11a DME NCT00676559   1     0, Withdrawn
Zimura Anti-C5 Aptamer) Polypoidal NCT02397954   2     5
AKB-9778 Tie-2 activator DME NCT02050828   2 144
AL-78898A Complement C3 inhibitor AMD NCT01157065   2   99
Volociximab α5β1 integrin antagonist AMD NCT00782093   1   63
JSM6427 α5β1 integrin antagonist AMD NCT00536016   1   36

Abbreviations: R= recruiting; AMD = neovascular age-related macular degeneration; DME = diabetic macular edema; PDR = proliferative diabetic retinopathy; RVO = retinal vein occlusion