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. Author manuscript; available in PMC: 2017 Jun 16.
Published in final edited form as: Semin Oncol. 2015 Sep 24;42(6):876–886. doi: 10.1053/j.seminoncol.2015.09.030

Table 2.

Early Molecular Responses with Frontline TKI Therapy and Associated Outcomes

Clinical Trial BCR-ABL1 3-month Landmark Analysis
6-month Landmark Analysis
Patients, n (%) PFS p OS p Patients (%) PFS p OS p


ENESTnd18 (4-year follow-up) Nilotinib 300 mg BID ≤ 10% 234 (91) 95% 0.06 97% 0.01 250 (97) 95% 0.06 96% 0.03
> 10% 24 (9) 83% 87% 7 (3) 75% 75%
Nilotinib 400 mg BID ≤ 10% 232 (89) 97% 0.04 97% 0.24 236 (93) 97% <0.01 97% <0.01
> 10% 28 (11) 89% 93% 17 (7) 82% 82%
Imatinib 400 mg QD ≤ 10% 176 (67) 98% <0.01 99% <0.01 216 (84) 97% <0.01 98% <0.01
> 10% 43 (16) 83% 84% 40 (16) 79% 70%
DASISION60 (3-year follow-up) Dasatinib 100 mg QD ≤ 10% 198 (84) 93% <0.01 96% 0.03 210 (89) 94% <0.01 97% <0.01
> 10% 37 (16) 68% 86% 26 (11) 66% 84%
Imatinib 400 mg QD ≤ 10% 154 (64) 96% <0.01 96% 0.04 197 (83) 95% <0.01 96% <0.01
> 10% 85 (36) 75% 88% 41 (17) 65% 88%

TKI, tyrosine kinase inhibitor; n, number; PFS, progression free survival; p, p value; OS, overall survival; BID, twice daily; QD, daily