| FA | Fanconi anemia |
| CRISPR/Cas9 | clustered regularly interspaced short palindromic repeats/Cas9 |
| BMF | bone marrow failure |
| ZFN | zinc-finger nucleases |
| TALEN | transcription activator-like effector nucleases |
| PARP | poly(ADP-ribose) polymerase |
| PARPi | PARP inhibition |
| gRNA | guide RNA |
| NHEJ | non-homologous endjoining |
| ODN | oligonucleotide donor |
| SNP | single-nucleotide polymorphisms |
| HDR | Homology directed repair |
| MMC | mitomycin-C |
| TERT | telomerase reverse transcriptase |
| HSPC | hematopoietic stem and progenitor cells |
| iPSC | Induced pluripotent stem cells |