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. 2017 Jun 14;18(6):1269. doi: 10.3390/ijms18061269
FA Fanconi anemia
CRISPR/Cas9 clustered regularly interspaced short palindromic repeats/Cas9
BMF bone marrow failure
ZFN zinc-finger nucleases
TALEN transcription activator-like effector nucleases
PARP poly(ADP-ribose) polymerase
PARPi PARP inhibition
gRNA guide RNA
NHEJ non-homologous endjoining
ODN oligonucleotide donor
SNP single-nucleotide polymorphisms
HDR Homology directed repair
MMC mitomycin-C
TERT telomerase reverse transcriptase
HSPC hematopoietic stem and progenitor cells
iPSC Induced pluripotent stem cells