Table 2.

Measurement tools used in the general assessment of mucopolysaccharidoses (MPS) patients.

	Type	Sections	Age groups	Assessor
Specific tools
MPS-PPM (Original) MPS-Physical Performance Measure	I	7 arm function tests 4 leg function tests 2 endurance tests
MPS-PPM (Modified) (Haley)	I	8 timed functional tests 2 endurance tests
MPS-HAQ MPS Health Assessment Questionnaire	All	52-item questionnaire	> 8 years	Caregivers
HS Focus Hunter Syndrome-Functional Outcomes for Clinical Understanding Scale	II	6 functional domains 2 additional domains Satisfaction Botheredness		Patient version Parent version
Generic tools
CHAQ Childhood Health Assessment Questionnaire		8 domains (30 items) Functional capacity Activities of daily living
CHQ Childhood Health Questionnaire		12 health concepts Physical and Psychosocial health status		Patient version Parent version – 2 additional concepts
HUI-3 Health Utilities Index-3		8 attributes describe patient experience of therapy the long-term outcomes of disease or therapy the efficacy of health care interventions the health status of general populations