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. 2017 Oct 26;8:566. doi: 10.3389/fneur.2017.00566

Table 5.

Cons and pros granulocyte colony-stimulating factor therapy in patients with Duchenne muscular dystrophy.

Pros Cons
Long-term study Open-label study—no control group
Objective functional testes Small number of study group
Qualification patients with different types of dystrophy and at every age Not a homogeneous group of study subjects
Lack of disqualification because the type of genome mutation Different functional states of patients (independent or wheelchair dependent)
Well-tolerated therapy Patients with or without steroids therapy