Table 5.
Cons and pros granulocyte colony-stimulating factor therapy in patients with Duchenne muscular dystrophy.
| Pros | Cons |
|---|---|
| Long-term study | Open-label study—no control group |
| Objective functional testes | Small number of study group |
| Qualification patients with different types of dystrophy and at every age | Not a homogeneous group of study subjects |
| Lack of disqualification because the type of genome mutation | Different functional states of patients (independent or wheelchair dependent) |
| Well-tolerated therapy | Patients with or without steroids therapy |