Table 2.
Change from baseline to week 12 in DGSSD (4-symptom composite scorea) and GEBT
Parameter | Placebo BID (n=88) | RM 10 μg BID (n=86) | RM 30 μg BID (n=91) | RM 100 μg BID (n=63) |
---|---|---|---|---|
Weekly Vomiting Episodes | ||||
Placebo | 10 μg | 30 μg | 100 μg | |
N=85 | N=81 | N=86 | N=66 | |
Baseline, mean ± SD | 5.7 ±6.0 | 7.7 ±17.2 | 6.9 ±10.3 | 4.8 ±5.2 |
Week 12, mean ± SD | 2.8 ±5.9 | 3.9 ±17.1 | 3.1 ±9.1 | 3.8 ±13.7 |
Change from baseline, mean ± SD | −2.9 ±5.8 | −3.7 ±12.5 | −3.8 ±7.6 | −1.1 ±13.5 |
Percent change from baselinea | −70.5% | −74.9% | −75.8% | −73.4 |
p-valueb (difference from placebo) | 0.36 | 0.25 | 0.59 | |
DGSSD 4 symptom composite scorec | ||||
Baseline, mean ± SD | 22.7 ± 7.3 | 22.7 ± 7.9 | 22.4 ± 6.7 | 24.0 ± 7.5 |
Week 12, mean ± SD | 17.1 ± 8.8 | 14.0 ± 10.3 | 13.8 ± 9.6 | 14.2 ± 9.5 |
Change from baseline, mean ± SD | −5.6 ± 8.8 | −8.7 ± 9.0 | −8.7 ± 9.0 | −9.7 ± 8.8 |
Change from baselined | −6.07 | −7.91 | −8.41 | −8.64 |
LS mean difference vs. placebo | −1.85 | −2.34 | −2.57 | |
p-value (difference from placebo)e | 0.134 | 0.053 | 0.052 | |
GEBT (T½ in min) | ||||
Baseline, mean ± SD | 127.1 ± 36.5 | 126.8 ± 37.6 | 128.6 ± 35.9 | 133.6 ± 35.4 |
Week 12, mean ± SD | 126.3 ± 39.8 | 112.8 ± 43.5 | 115.8 ± 45.7 | 118.0 ± 49.5 |
Change from baseline, mean ± SD | −0.0 ± 38.5 | −12.7 ± 38.1 | −12.8 ± 36.5 | −13.6 ± 40.5 |
Change from baseline | −0.43 | −13.36 | −12.55 | −12.47 |
LS mean difference vs. placebo | −12.93 | −12.12 | −12.04 | |
95% CI of difference | −24.04; −1.82 | −22.92; −1.33 | −24.11; 0.04 | |
p-value (difference from placebo)b | 0.023 | 0.028 | 0.051 |
BID, twice daily; CI = confidence interval; DGSSD, Diabetic Gastroparesis Symptom Severity Diary; GEBT, gastric emptying breath test; LS, least squares; RM, relamorelin; SD, standard deviation
Analysis was done on log-transformed change-from-baseline of weekly least square means for vomiting data, and reported as percent change from baseline.
Two-sided p-value from longitudinal, mixed-effects model with repeated measures, including fixed effects for treatment, week, treatment-by-week interaction, as well as baseline and baseline-by-week interaction values as the covariates with unstructured variance-covariance correlation matrix being common to all subjects for the repeated measures over treatment weeks
Nausea, post-prandial fullness, abdominal pain, bloating; composite score in total numeric points;
Analysis done on change-from-baseline data for sum of weekly averages of 4 individual symptom scores (nausea, abdominal pain, post-prandial fullness, and bloating);