Table 1.

Surgical and Injection Data

		Age (Years)	Volume	Vector Genomes	Injection Number	Follow-up
First cohort	CG01	28	330 μL	2.01 × 1010	2	1 year
	BJ03	27	200 μL	1.22 × 1010	3	1 year
	MM04a	35	300 μL	1.83 × 1010	3	3 years 5 months
Second cohort	MR05a	42	700 μL	4.27 × 1010	5	2 years
	HM06a	22	770 μL	4.7 × 1010	2	3 years
	HT07a	20	530 μL	3.23 × 1010	4	3 years 2 months
Third cohort	AM08a	19	700 μL	4.27 × 1010	4	2 years 6 months
	HM09	15	800 μL	4.8 × 1010	4	1 year
	LC10a	9	770 μL	4.7 × 1010	3	2 years 2 months

^aPatients who underwent long-term follow-up.