Table 1.
Definitions of terminology used in the current study
Term | Definition |
---|---|
Drugs for rare diseases (DRDs) | Drugs used to treat diseases that affect ≤ 50 per 100,000 people. |
Drugs for ultra-rare diseases (DURDs) | Drugs used to treat diseases that affect ≤ 1 per 100,000 people. - |
Drugs for other rare diseases (DORDs) | Drugs used to treat rare diseases that affect > 1 to 50 per 100,000 people. |