Table 1. List of the ONs employed in this study.
Names | Target | Sequences |
---|---|---|
SSO-654 | Mutant β-globin | 5′-GcTaTtAcCtTaAcCc-3′ |
Control ASO (SPC 3046) | Non targeting | 5′-mCGmCAgattataaAmCmCt-3′ |
BCL2-ASO (SPC2996) | BCL-2 | 5′-mCTcccagcgtgcgmCmCa-3′ |
Cy5-ASO | BCL-2 | 5′-Cy5-mCTcccagcgtgcgmCmCa-3′ |
β-Cat-ASO (EZN-3889) | β-Catenin | 5′-CCAtcttgtgatcCAT-3′ |
AR-ASO (EZN-4176) | Androgen Receptor | 5′-ACCaagtttcttcAGC-3′ |
m = methyl.
Capital letters = LNA.
All ON are all-phosphorothioate.