Table 1.

Patient Characteristics at Baseline (Safety Analysis Set)

Age (years)	50 (32‐72)
Sex (M:F)	1/28
Weight (kg)	63 (48‐92)
Disease duration (years)	5.3 (1.2‐21.2)
Liver function tests
ALP (IU/L)	417 (163‐834)
ALT (IU/L)	83 (36‐269)
AST (IU/L)	61 (32‐171)
γGT (IU/L)	292 (60‐1277)
Total bilirubin (μmol/L)	12 (4‐45)

Values are expressed as median (range). Normal ranges: ALP 40‐129 IU/L (men), 35‐104 IU/L (women); ALT 10‐50 IU/L (men), 10‐35 IU/L (women); AST 0‐37 IU/L (men), 0‐31 IUL/L (women); γGT 10‐71 IU/L (men), 6‐42 IU/L (women); total bilirubin 0‐20 μmol/L.