CRISPR |
clustered regularly interspaced short palindromic repeats |
C7 |
type VII collagen |
TALEN |
transcription activator like effector nucleases |
HDR |
homology directed repair |
UCB |
umbilical cord blood |
HSC |
hematopoietic stem cells |
GVHD |
graft versus host disease |
gRNA |
Guide RNA |
indel |
insertions/deletions |
ICE |
Inference of CRISPR Edits |
RNP |
ribonucleoprotein |
MOI |
multiplicity of infection |
CFU |
colony forming unit |
AAV |
Adeno-associated virus |
SA |
splice acceptor |
UCOE |
ubiquitous chromatin opening element |
tEGFR |
truncated epidermal growth factor receptor gene |
UMET |
UCOE.MND.tEGFR.T2A |
NC |
non-collagenase domain |
KC |
keratinocytes |