| CRISPR | clustered regularly interspaced short palindromic repeats |
| C7 | type VII collagen |
| TALEN | transcription activator like effector nucleases |
| HDR | homology directed repair |
| UCB | umbilical cord blood |
| HSC | hematopoietic stem cells |
| GVHD | graft versus host disease |
| gRNA | Guide RNA |
| indel | insertions/deletions |
| ICE | Inference of CRISPR Edits |
| RNP | ribonucleoprotein |
| MOI | multiplicity of infection |
| CFU | colony forming unit |
| AAV | Adeno-associated virus |
| SA | splice acceptor |
| UCOE | ubiquitous chromatin opening element |
| tEGFR | truncated epidermal growth factor receptor gene |
| UMET | UCOE.MND.tEGFR.T2A |
| NC | non-collagenase domain |
| KC | keratinocytes |