In the 1990s it was well documented that some patients who initially responded to
cancer immunotherapies with interleukin-2 or tumor infiltrating lymphocyte
adoptive cell transfer therapy may develop acquired resistance through loss of
B2M, which leads to absence of surface expression of HLA
class I. More recently, we identified defects in B2M from patients with acquired
resistance to immune checkpoint blockade, along with defects in interferon
signaling (JAK1, JAK2). Interferon signaling activates transcription of antigen
processing machinery. Two in vitro and one in vivo CRISPR based screens have
identified APLNR, PTPN2 and PBAF as immunotherapy targets, and each is a
regulator of interferon signaling, and thereby each indirectly impacts
downstream antigen presentation. The CRISPR screens also identified components
of antigen processing machinery (e.g. TAP1, TAP2, and immunoproteasome subunits
including PSMB9) as determinants of sensitivity to immunotherapy. NLRC5, a
transcriptional regulator of MHC-I expression, has also been implicated in
immunotherapy sensitivity in the CRISPR based screens. The work reported by
Huang, et al. (1) in this issue of
Clinical Cancer Research identifies MEX3B as a post-transcriptional regulator of
HLA-A, via binding and disruption of the 3′UTR of the HLA-A mRNA.