Table 4.
Hematology Measures at Baseline and after rAAVrh74.MCK.GALGT2 Treatment
| Time | Subject | WBC (K/mm3) | RBC (M/mm3) | HGB (g/dL) | HCT (%) | MCV (fL) | MCH (pg) | MCHC (%) | RDW (%) | PLC (K/mm3) | MPV (fL) | Neut (%) | Lymph (%) | Mono (%) | EOS (%) | BAS (%) |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Baseline | 07D147 | 4.2 | 5.06 | 11.7 | 37.1 | 73.3 | 23.1 | 31.5 | 13.3 | 284 | 11.5 | 47 | 45 | 8 | 0 | 1 |
| 04C034 | 6.2 | 5.94 | 12.9 | 42.7 | 71.9 | 21.7 | 30.2 | 12.2 | 381 | 10.4 | 71 | 23 | 0 | 0 | 0 | |
| 24 hr | 07D147 | 4 | 3.67 | 8.5 | 26.5 | 72.2 | 23.2 | 32.1 | 13.3 | 128 | 12.3 | 77 | 19 | 2 | 0 | 2 |
| 04C034 | 5.2 | 3.67 | 8.0 | 26.3 | 71.7 | 21.8 | 30.4 | 12.4 | 218 | 11.2 | 73 | 16 | 10 | 1 | 0 | |
| 48 hr | 07D147 | 4.6 | 3.16 | 7.3 | 23.4 | 74.1 | 23.1 | 31.2 | 13.4 | 157 | 11.6 | 52 | 37 | 7 | 0 | 3 |
| 04C034 | 3.3 | 3.56 | 7.6 | 25.8 | 72.5 | 21.3 | 29.5 | 12.1 | 222 | 11.0 | 53 | 29 | 9 | 9 | 0 | |
| 1 month | 07D147 | 4.1 | 5.71 | 12.9 | 42.4 | 74.3 | 22.6 | 30.4 | 13.2 | 296 | 10.6 | 49 | 45 | 6 | 0 | 0 |
| 04C034 | 5.2 | 5.91 | 12.8 | 42.2 | 71.4 | 21.7 | 30.3 | 12.5 | 297 | 11.5 | 68 | 25 | 6 | 0 | 1 | |
| 2 months | 07D147 | 4.4 | 6.18 | 13.7 | 45.2 | 73.1 | 22.2 | 30.3 | 13.2 | 256 | 10.7 | 48 | 46 | 6 | 0 | 0 |
| 04C034 | 5.5 | 6.11 | 13.3 | 43.2 | 70.7 | 21.8 | 30.8 | 12.2 | 426 | 10.2 | 63 | 32 | 4 | 0 | 0 | |
| 3 months | 07D147 | 3.4 | 5.67 | 13 | 40 | 70.5 | 22.9 | 32.5 | 13.5 | 240 | 11.7 | 43 | 49 | 8 | 1 | 0 |
| 04C034 | 8.2 | 6.26 | 13.5 | 43.5 | 69.5 | 21.6 | 31 | 12.8 | 193 | 11.5 | 64 | 30 | 5 | 0 | 0 |
WBC, white blood cell; RBC, red blood cell; HGB, hemoglobin; HCT, hematocrit; MCV, mean corpuscular volume; MCH, mean corpuscular hemoglobin; MCHC, mean corpuscular hemoglobin concentration; RDW, red cell distribution width; PLC, platelet count; MPV, mean platelet volume; Neut, neutrophils (relative); Lymph, lymphocytes (relative); Mono, monocytes (relative); EOS, eosinophils (relative); BAS, basophils (relative).