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. 2014 Dec 4;1(2):173–184. doi: 10.2217/mmt.14.20

Table 1. . Phase II and III paclitaxel trials in melanoma.

Study (author) Treatment arms Number per arm ORR (CR/PR) CRR (CR/PR/SD) Median PFS/TTP Median OS Ref.
Phase II P single agent (Walker et al.) P 80 mg/m2, 3 weeks on, 1 week off 27 0% 30% PFS: 1.8 months 7.6 months [26]

Phase II P single agent (Einzig et al.) P 250 mg/m2 every 21 days 34 14% [27]

Randomized Phase II P vs P plus carboplatin (Zimpfer-Rechner et al.) P 80 mg/m2 every week for 6 weeks, repeated every 8 weeks 18 0% 28% TTP: 54 days 218 days [28]
  P 80 mg/m2 and carboplatin 200 mg/m2 every week for 6 weeks, repeated every 8 weeks 16 0% 19% TTP: 57 days 209 days  

Phase II, randomized, double-blind trial of P ± elesclomol (O’Day et al.) P 80 mg/m2, 3 weeks on, 1 week off 28 3.6% 39.3% PFS: 1.8 months (95% CI: 1.6–3.4) 7.8 months [29]
  P 80 mg/m2 plus eclesclomol 213 mg/m2, 3 weeks on, 1 week off 53 15.1% 62.3% PFS: 3.7 months (95% CI: 2.5–5.5) 11.9 months  

Phase III SYMMETRY study; randomized, double-blind trial of P ± elesclomol (O’Day et al.)§ P 80 mg/m2, 3 weeks on, 1 week off 326 4% 18% PFS: 1.9 months 11.4 months [25]
  P 80 mg/m2 plus eclesclomol 213 mg/m2, 3 weeks on, 1 week off 325 7% 22% PFS: 3.4 months 10.6 months  

Trial stopped early due to ORR of <10%.

Crossover allowed.

§Trial closed early due to the finding of an imbalance in total deaths favoring paclitaxel, predominantly in patients with high lactate dehydrogenase levels.

CR: Complete response; CRR: Clinical response rate; ORR: Overall response rate; OS: Overall survival; P: Weekly paclitaxel; PFS: Progression-free survival; PR: Partial response; SD: Stable disease; TTP: Time to progression.