Table 2.
Efficacy results in the intent‐to‐treat population according to treatment groupa
Sarilumab | |||
---|---|---|---|
Placebo plus csDMARD(s) (n = 181) | 150 mg every 2 weeks plus csDMARD(s) (n = 181) | 200 mg every 2 weeks plus csDMARD(s) (n = 184) | |
Signs and symptoms | |||
ACR20 at week 24, no. (%)b | 61 (33.7) | 101 (55.8)c | 112 (60.9)c |
ACR50 at week 24, no. (%)b | 33 (18.2) | 67 (37.0)c | 75 (40.8)c |
ACR70 at week 24, no. (%)b | 13 (7.2) | 36 (19.9)d | 30 (16.3)e |
ACR core set of disease activity measures, adjusted mean change from baseline at week 24 ± SE | |||
SJC (66 assessed)f | −8.2 ± 0.72 | −11.6 ± 0.69e | −11.9 ± 0.67c |
TJC (68 assessed)f | −10.6 ± 1.06 | −14.4 ± 1.02d | −17.0 ± 0.99c |
Patient's global assessment (0–100 mm VAS)f | −19.8 ± 2.17 | −29.6 ± 2.05d | −31.3 ± 2.00c |
Physician's global assessment (0–100 mm VAS)f | −28.6 ± 1.81 | −40.7 ± 1.70c | −43.2 ± 1.65c |
Patient's assessment of pain (0–100 mm VAS)f | −21.3 ± 2.25 | −31.9 ± 2.09d | −33.7 ± 2.04c |
HAQ DIf | −0.3 ± 0.05 | −0.5 ± 0.05e | −0.6 ± 0.05d |
CRP, mg/literf | −3.6 ± 1.56 | −15.2 ± 1.46c | −23.3 ± 1.42c |
DAS28‐CRP, adjusted mean change from baseline at week 24 ± SEb | −1.4 ± 0.12 | −2.4 ± 0.11c | −2.8 ± 0.11c |
DAS28‐CRP response at week 24, no. (%) | |||
<2.6b | 13 (7.2) | 45 (24.9)c | 53 (28.8)c |
≤3.2f | 25 (13.8) | 59 (32.6)c | 74 (40.2)c |
Physical function | |||
HAQ DI, adjusted mean change from baseline at week 12 ± SEb | −0.26 ± 0.04 | −0.46 ± 0.04d | −0.47 ± 0.04d |
HAQ DI response at week 24, no. (%)f | |||
Change ≥0.22 | 64 (35.4) | 86 (47.5)g | 103 (56.0)c |
Change ≥0.30 | 57 (31.5) | 78 (43.1)g | 87 (47.3)e |
Each selected sarilumab dose regimen was tested versus placebo at a significance level of 0.025 (with Bonferroni adjustment for multiple comparisons). csDMARD(s) = conventional synthetic disease‐modifying antirheumatic drug(s); ACR20 = American College of Rheumatology 20% criteria for improvement; VAS = visual analog scale.
End point in predefined hierarchy.
P < 0.0001 versus placebo plus csDMARD(s).
P < 0.001 versus placebo plus csDMARD(s).
P < 0.01 versus placebo plus csDMARD(s).
In the 2 sarilumab groups, the benchmark was not included in the predefined hierarchy for the swollen joint count (SJC), tender joint count (TJC), patient's global assessment, physician's global assessment, patient's global assessment of pain, Health Assessment Questionnaire disability index (HAQ DI), C‐reactive protein (CRP) level, change from baseline in the Disease Activity Score in 28 joints (DAS28) using the CRP level, DAS28‐CRP response at week 24 of ≤3.2, and change in HAQ DI response at week 24. Nominal P values are provided.
= P < 0.05 versus placebo plus csDMARD(s).