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. 2018 Oct 11;13:596–604. doi: 10.1016/j.omtn.2018.10.004

Table 1.

Selected PMO Sequences for DYSF Exon 28–29 Skipping

DYSF Exon to Skip Oligo Name Distance from Acceptor Splice Site Oligo Sequence (5′ to 3′) Predicted Skip (%)
28 Ac7 7 ACTCAATGTCATCCTTGGGAAGCACCTTCT 70.52
28 Ac11 11 GGGCACTCAATGTCATCCTTGGGAAGCACC 68.21
28 Ac41 41 CATTCCTCATCTTCCCACTTCCAGCCCAGT 61.01
29 Ac36 36 TCTTCTCAGCAGGGACCCAGTGCTTCGGCT 86.38
29 Ac32 32 CTCAGCAGGGACCCAGTGCTTCGGCTTCCG 79.7
29 Ac40 40 TACATCTTCTCAGCAGGGACCCAGTGCTTC 62.06