Table 1.
Selected PMO Sequences for DYSF Exon 28–29 Skipping
DYSF Exon to Skip | Oligo Name | Distance from Acceptor Splice Site | Oligo Sequence (5′ to 3′) | Predicted Skip (%) |
---|---|---|---|---|
28 | Ac7 | 7 | ACTCAATGTCATCCTTGGGAAGCACCTTCT | 70.52 |
28 | Ac11 | 11 | GGGCACTCAATGTCATCCTTGGGAAGCACC | 68.21 |
28 | Ac41 | 41 | CATTCCTCATCTTCCCACTTCCAGCCCAGT | 61.01 |
29 | Ac36 | 36 | TCTTCTCAGCAGGGACCCAGTGCTTCGGCT | 86.38 |
29 | Ac32 | 32 | CTCAGCAGGGACCCAGTGCTTCGGCTTCCG | 79.7 |
29 | Ac40 | 40 | TACATCTTCTCAGCAGGGACCCAGTGCTTC | 62.06 |