Fig. 2.
This figure demonstrates several different approaches for targeted treatment: modifying epigenetic repression of DUX4, targeting DUX4 mRNA, DUX4 protein, or cellular downstream effects of DUX4 expression
This figure demonstrates several different approaches for targeted treatment: modifying epigenetic repression of DUX4, targeting DUX4 mRNA, DUX4 protein, or cellular downstream effects of DUX4 expression