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. Author manuscript; available in PMC: 2020 Jan 1.
Published in final edited form as: Immunol Rev. 2019 Jan;287(1):103–120. doi: 10.1111/imr.12714

Table 2.

Autoantigens in APECED patients and their associated disease manifestation.

Autoantigen Tissue of origin Associated clinical manifestation
IFN-ω Cytokine APECED, Thymoma, Myasthenia gravis,
RAG deficiency
IFN-α Cytokine APECED (protection from type 1
diabetes?), Thymoma, Myasthenia gravis,
RAG deficiency
IFN-β Cytokine Unclear
IFN-λ Cytokine Unclear
IL-6 Cytokine Unclear
IL-17A Cytokine Chronic mucocutaneous candidiasis
IL-17F Cytokine Chronic mucocutaneous candidiasis
IL-22 Cytokine Chronic mucocutaneous candidiasis
NACHT leucine-rich-repeat protein 5
(NALP5)
Parathyroid, ovary, breast, testis Hypoparathyroidism
Calcium-sensing receptor (CaSR) Parathyroid, pancreas, kidney Hypoparathyroidism
21-hydroxylase (CYP21A2) Adrenal gland Primary adrenal insufficiency
17-α-hydroxylase (CYP17A1) Adrenal gland Primary adrenal insufficiency, ovarian
failure
Thyroglobulin (TG) Thyroid Hypothyroidism
Thyroid peroxidase (TPO) Thyroid Hypothyroidism
Islet antigen-2 (IA-2) Pancreas Type I diabetes
Potassium channel-regulating protein
(KCNRG)
Lung, cervix Autoimmune pneumonitis
Bactericidal/permeability-increasing fold-
containing B1 (BPIFB1)
Lung, stomach, esophagus, cervix Autoimmune pneumonitis
Aromatic L-amino acid decarboxylase
(AADC)
Kidney, intestine, brain, liver,
pancreas
Autoimmune hepatitis, vitiligo
Cytochrome P450 1A2 (CYP1A2) Liver Autoimmune hepatitis
CYP2A6 Liver Autoimmune hepatitis
Tryptophan hydroxylase (TPH) Multiple Intestinal dysfunction, autoimmune
hepatitis, autoimmune gastritis
Hydrogen-Potassium ATPase Stomach Autoimmune gastritis
Intrinsic factor Stomach Pernicious anemia
Glutamic acid decarboxylase (GAD65) Pancreas, brain Intestinal dysfunction, vitiligo
Histidine decarboxylase (HDC) Brain, stomach, lung Intestinal dysfunction
Defensin, alpha 5 (DEFA5) Paneth cells Intestinal dysfunction
Side chain cleavage enzyme (CYP11A1) Adrenal, ovary, testis Primary adrenal insufficiency, ovarian
failure, testicular failure
Transglutaminase 4 Prostate Prostatitis (male infertility)
Testis-specific gene 10 protein (TSGA10) Testis, brain Unclear
Tudor domain containing protein 6 (TDRD6) Testis, brain Hypopituitarism (growth hormone
deficiency)
Melanoma antigen family B 2 (MAGEB2) Testis, female germ cells Unclear
Protein disulfide isomerase-like testis
(PDILT)
Testis Unclear
Tyrosine hydroxylase (TH) Brain, adrenal Alopecia, enamel hypoplasia
SOX9/SOX10 Nervous system, breast Vitiligo
Myelin protein 0 Nervous system Neuropathy
Interphotoreceptor retinoid‐binding protein Retina Retinitis pigmentosa