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. Author manuscript; available in PMC: 2020 May 1.
Published in final edited form as: Pediatr Blood Cancer. 2019 Jan 22;66(5):e27614. doi: 10.1002/pbc.27614

TABLE 3.

Disease Complication Responses to Sirolimus Treatment for GLA and GSD Patients

Complication Response GLA, n GSD, n Total, n (%)
Pleural Effusion 6 1 7
 Complete Resolution 2 0 2 (28.5)
 Partial Improvement 3 0 3 (43)
 No Improvement 1 1 2 (28.5)
 Progressive Disease 0 0 0
Pericardial Effusion 3 1 4
 Complete Resolution 2 0 2 (50)
 Partial Improvement 0 0 0
 No Improvement 1 1 2 (50)
 Progressive Disease 0 0 0
Bone Involvement 11 5 16
 Complete Resolution 1 0 1 (6)
 Partial Improvement 7 3 10 (63)
 No Improvement 3 2 5 (31)
 Progressive Disease 0 0 0