Table 1.
Summary of subject demographics and baseline characteristics
| Assessment | Statistic | Study | Overall | ||
|---|---|---|---|---|---|
| 1 | 2 | 3 | |||
| Number of subjects (%) | 3 (13) | 8 (35) | 12 (52) | 23 (100) | |
| Age, years | Mean (SD) | 13.3 (10.4) | 3.3 (1.2) | 15.5 (5.5) | 11.0 (7.7) |
| Median (range) | 9.4 (5.5–25.1) | 3.2 (1.7–5.0) | 14.0 (8.5–25.3) | 10.1 (1.7–25.3) | |
| Baseline body weight, kg | Mean (SD) | 44.7 (30.4) | 13.3 (2.6) | 52.2 (26.2) | 37.7 (27.7) |
| Median (range) | 34.6 (20.6–78.8) | 13.5 (9.4–17.4) | 51.2 (15.0–104.0) | 24.8 (9.41–104.0) | |
| Sex [n (%)] | Female | 1 (33) | 3 (38) | 8 (67) | 12 (52) |
| Male | 2 (67) | 5 (62) | 4 (33) | 11 (48) | |
| Race [n (%)] | Asian | 1 (33) | 2 (25) | – | 3 (13) |
| Black | – | 1 (12) | – | 1 (4) | |
| Other | – | 2 (25) | 3 (25) | 5 (22) | |
| White | 2 (67) | 3 (38) | 9 (75) | 14 (61) | |
SD standard deviation