Table 4.
Discriminative power: t tests comparing the mean scores of child outcomes (PedsQL™, HUI-3, Vineland-II, CBCL) for domain responses on caregiver preference-weighted instruments, n = 224
| Caregiver quality of life measures | n (%)a | Child outcomes [mean (SD)] | |||
|---|---|---|---|---|---|
| PedsQL™ b | HUI-3b | Vineland-IIb | CBCLb | ||
| SF-6D domains | |||||
| Physical functioning | |||||
| No problems | 193 (87) | 64.2 (15.6)* | 0.664 (0.24) | 68.6 (11.5) | 63.3 (9.3) |
| At least some problems | 28 (13) | 55.3 (15.5)* | 0.616 (0.20) | 66.8 (7.9) | 67.2 (9.6) |
| Role limitations | |||||
| No limitations | 112 (51) | 66.5 (16.4)* | 0.699 (0.20)* | 70.4 (10.9)* | 62.3 (10.0)* |
| At least some limitations | 106 (49) | 59.6 (14.6)* | 0.613 (0.26)* | 66.2 (11.3)* | 65.3 (8.7)* |
| Social functioning | |||||
| No problems | 91 (42) | 67.3 (16.1)* | 0.691 (0.23) | 68.9 (11.4) | 61.4 (9.7)* |
| At least some problems | 128 (58) | 59.8 (14.7)* | 0.632 (0.24) | 68.0 (11.1) | 65.8 (8.8)* |
| Pain | |||||
| No pain | 109 (50) | 66.9 (16.4)* | 0.693 (0.23)* | 69.4 (11.2) | 62.2 (9.6)* |
| At least some pain | 111 (50) | 59.3 (14.3)* | 0.621 (0.24)* | 67.4 (11.1) | 65.5 (9.07)* |
| Mental health | |||||
| No problems | 35 (16) | 69.8 (13.4)* | 0.754 (0.18)* | 69.5 (9.8) | 59.3 (9.5)* |
| At least some problems | 183 (84) | 61.7 (15.8)* | 0.641 (0.24)* | 68.2 (11.5) | 64.6 (9.2)* |
| Vitality | |||||
| No or some problems | 76 (35) | 69.4 (15.6)* | 0.697 (0.23) | 69.6 (12.1) | 59.4 (10.4)* |
| Moderate or severe problems | 143 (65) | 60.0 (14.8)* | 0.636 (0.23) | 67.7 (10.7) | 66.1 (8.0)* |
| EQ-5D-3L domains | |||||
| Mobility | |||||
| No problems | 205 (93) | 63.2 (15.6) | 0.657 (0.24) | 68.3 (11.3) | 63.7 (9.6) |
| At least some problems | 15 (7) | 61.0 (16.8) | 0.666 (0.18) | 68.9 (10.0) | 64.3 (7.8) |
| Self-care | |||||
| No problems | 215 (98) | 63.0 (15.5) | 0.657 (0.24) | 68.3 (11.2) | 63.9 (9.4) |
| At least some problems | 5 (2) | 63.0 (25.4) | 0.701 (0.16) | 75.0 (14.0) | 59.0 (12.1) |
| Usual activities | |||||
| No problems | 184 (84) | 64.3 (15.7)* | 0.673 (0.23)* | 68.7 (11.3) | 63.5 (9.4) |
| At least some problems | 36 (16) | 55.8 (14.1)* | 0.581 (0.24)* | 66.7 (10.8) | 65.7 (9.5) |
| Pain/discomfort | |||||
| No problems | 121 (55) | 64.5 (15.8) | 0.670 (0.24) | 68.6 (11.2) | 63.7 (10.1) |
| At least some problems | 99 (45) | 61.3 (15.4) | 0.643 (0.23) | 67.9 (11.2) | 63.9 (8.7) |
| Anxiety/depression | |||||
| No problems | 107 (49) | 66.3 (16.1)* | 0.718 (0.21)* | 70.0 (11.3) | 61.4 (10.3)* |
| At least some problems | 112 (51) | 59.5 (14.5)* | 0.601 (0.25)* | 66.8 (10.9) | 66.1 (7.9)* |
Higher scores on the CBCL indicate worse problems; higher scores on the PedsQL™, HUI-3, and Vineland-II indicate better functioning/health
CBCL Child Behavior Checklist, EQ-5D-3L three-level EuroQoL-5 Dimension, HUI-3 Health Utilities Index Mark 3, PedsQL™ Pediatric Quality of Life Inventory™, SF-6D Short Form-6 Dimension, Vineland-II Vineland Adaptive Behavior Scales Second Edition
*p < 0.05 using a Bonferroni correction factor such that groups with two, three, or four levels must exhibit a p value of 0.0500, 0.0167, and 0.0083, respectively
an values may not total to 224 due to missing responses
bCaregiver-reported child measure