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| Methods | No information provided. |
| Participants | 10 children with infantile‐onset Pompe disease. |
| Interventions | Myozyme® treatment at 40 mg/kg every week compared to 20 mg/kg every other week for ≥ 1 year. |
| Outcomes | Survival, ventilator‐free survival, left ventricular mass index, motor outcome and infusion‐associated reactions. |
| Notes |
