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. 2018;89(Suppl 11):5–39. doi: 10.23750/abm.v89i11-S.7988

Table 7.

Hypomethylating therapy of MDS and AML real life studies

References Therapy Patients (n) Responses (%) Responses time median (range) Median OS (months) Median PFS (months)
MDS
Fenaux, 2009 (42) Azacitidine 75 mg/m2/7days 179 pts 17% CR/12% PR/10% HI 2 cycles (1-16) 24,5 17,8
Voso, 2013 (40) 196 pts 19% CR/17% PR/21% HI 4,5 cycles (7-15) 17,1 -
Sebert, 2017 (53) 702 pts MDS/AML 44% ORR/15% CR - 14,9 -
AML
Dombret, 2015 (46) Azacitidine 75 mg/m2/7days 236 pz 28% CR/CRi - 10,4
12,1*
9,3
Pleyer, 2017 (58) 193 pz 19% CR/CRi/PR - 10,7 13,8
Kantarjian, 2012 (49) Decitabine 20 mg/m2/5days 242 pz 18% CR/CRp 4,3 months 7,7 8,5
Blum, 2010 (50) Decitabine 20 mg/m2/10days 53 pz 64% CR/CRi 3 cycles (1-6) 14 12

* Post-hoc analysis: time to the next treatment

CR = complete remission; CRi = CR with complete haematological recovery; PR = partial remission; HI = haematological improve¬ment; OS = overall survival; PFS: progression-free survival