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. 2019 Mar 8;37(3):538–547. doi: 10.1007/s10637-019-00755-x

Table 3.

Efficacy outcomes

Best overall response All (N = 25) Percent 95% CI
CR 3 12.0 2.6–31.2
PR 17 68.0 46.5–85.1
LSD 1 4.0 0.1–20.4
SD 1 4.0 0.1–20.4
PD 2 8.0 1.0–26.0
NE 1 4.0 0.1–20.4
ORR (CR + PR) 20 80.0 59.3–93.2
CBR (CR + PR + LSD) 21 84.0 63.9–95.5
DCR (CR + PR + LSD + SD) 22 88.0 68.8–97.5

CI confidence interval, CR complete response, PR partial response, LSD long-term stable disease ≥24 weeks, SD stable disease <24 weeks, PD progressive disease, NE not evaluable, ORR overall response rate, DCR disease control rate, CBR clinical benefit rate